Gene therapy company Spark Therapeutics inks licensing deal for a retinitis pigmentosa gene therapy
Retinitis pigmentosa is the most common inherited eye disease. Mutations in the gene for rhodopsin, the pigment for photoreceptor cells in the retina responsible for the perception of light, account for 15 percent of retinitis pigmentosa cases. CHOP spinout Spark Therapeutics, which has a late stage retinitis pigmentosa gene therapy treatment under development, is collaborating […]